Breaking barriers in clinical trials and FDA approval to deliver therapies to families by 2025.
There is additional essential work to be done to pave the way for successful clinical trials and the approval of effective therapies.
With every affected patient in mind, our Therapeutic Accelerator program seeks to overcome the hurdles and shorten the timeline to get therapies to our families.
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As a FSHD (facioscapulohumeral muscular dystrophy) patient advocate, I am excited to see this initiative announced, which will help to ensure that the patient experience is incorporated into the development and access of medicines and improving our healthcare.
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